
6 Human Neuron Core, Rosamund Stone Zander Translational Neuroscience Center, Boston Children's Hospital, Boston, MA 02115, USA Department of Neurology, Boston Children's Hospital, Boston, MA 02115, USA.5 Lewis-Sigler Institute for Integrative Genomics, Princeton University, Princeton, NJ 08544, USA.4 Department of Pediatrics, University of Minnesota, Minneapolis, MN 55454, USA Center for Genome Engineering, University of Minnesota, Minneapolis, MN 55108, USA Stem Cell Institute, University of Minnesota, Minneapolis, MN 55455, USA.
3 Department of Molecular Biology, Princeton University, Princeton, NJ 08544, USA.
2 Department of Cellular and Molecular Pharmacology, University of California, San Francisco, San Francisco, CA 94158, USA Department of Microbiology and Immunology, University of California, San Francisco, San Francisco, CA 94158, USA Howard Hughes Medical Institute, University of California, San Francisco, San Francisco, CA 94158, USA Whitehead Institute for Biomedical Research, Massachusetts Institute of Technology, Cambridge, MA 02142, USA. 1 Merkin Institute of Transformative Technologies in Healthcare, Broad Institute of Harvard and MIT, Cambridge, MA 02141, USA Department of Chemistry and Chemical Biology, Harvard University, Cambridge, MA 02138, USA Howard Hughes Medical Institute, Harvard University, Cambridge, MA 02138, USA.